Breton, C, Clark, PM, Wang, LL, Greig, JA, Wilson, JM ITR-Seq, a next-generation sequencing assay, identifies genome-wide DNA editing sites in vivo following adeno-associated viral vector-mediated genome editing , bmc genomics, 21(1): 2020

Somanathan, S, Calcedo, R, Wilson, JM Adenovirus-Antibody Complexes Contributed to Lethal Systemic Inflammation in a Gene Therapy Trial , molecular therapy, 28(3): 2020,784-793

Wang, LL, Yang, Y, Breton, C, Bell, P, Li, MY, Zhang, J, Che, Y, Saveliev, A, He, ZN, White, J, Latshaw, C, Xu, CY, McMenamin, D, Yu, HW, Morizono, H, Batshaw, ML, Wilson, JM A mutation-independent CRISPR-Cas9-mediated gene targeting approach to treat a murine model of ornithine transcarbamylase deficiency , science advances, 6(7): 2020

Hinderer, C, Katz, N, Dyer, C, Goode, T, Johansson, J, Bell, P, Richman, L, Buza, E, Wilson, JM Translational Feasibility of Lumbar Puncture for Intrathecal AAV Administration , molecular therapy-methods & clinical development, 17: 2020,969-974

Wang, LL, Yang, Y, Breton, CA, White, J, Zhang, J, Che, Y, Saveliev, A, McMenamin, D, He, ZN, Latshaw, C, Li, MY, Wilson, JM CRISPR/Cas9-mediated in vivo gene targeting corrects hemostasis in newborn and adult factor IX-knockout mice , blood, 133(26): 2019,2745-2752

Ashley, SN, Somanathan, S, Giles, AR, Wilson, JM TLR9 signaling mediates adaptive immunity following systemic AAV gene therapy , cellular immunology, 346: 2019

Hordeaux, J, Hinderer, C, Buza, EL, Louboutin, JP, Jahan, T, Bell, P, Chichester, JA, Tarantal, AF, Wilson, JM Safe and Sustained Expression of Human Iduronidase After Intrathecal Administration of Adeno-Associated Virus Serotype 9 in Infant Rhesus Monkeys , human gene therapy, 30(8): 2019,957-966

Hordeaux, J, Yuan, Y, Clark, PM, Wang, Q, Martino, RA, Sims, JJ, Bell, P, Raymond, A, Stanford, WL, Wilson, JM The GPI-Linked Protein LY6A Drives AAV-PHP.B Transport across the Blood-Brain Barrier , molecular therapy, 27(5): 2019,912-921

Giles, AR, Sims, JJ, Turner, KB, Govindasamy, L, Alvira, MR, Lock, M, Wilson, JM Deamidation of Amino Acids on the Surface of Adeno-Associated Virus Capsids Leads to Charge Heterogeneity and Altered Vector Function , molecular therapy, 26(12): 2018,2848-2862

Greig, JA, Nordin, JML, Smith, MK, Ashley, SN, Draper, C, Zhu, YQ, Bell, P, Buza, EL, Wilson, JM A Gene Therapy Approach to Improve Copper Metabolism and Prevent Liver Damage in a Mouse Model of Wilson Disease , human gene therapy clinical development, 30(1): 2019,29-39