Selected Publications
Mowad TG, Willett AE, Mahmoudian M, Lipin M, Heinecke A, Maguire AM, Bennett J, Ashtari M: Compensatory Cross-Modal Plasticity Persists After Sight Restoration.
Front Neurosci 12 (14): 291,2020.
Maguire, Albert M; Russell, Stephen; Wellman, Jennifer A; Chung, Daniel C; Yu, Zi-Fan; Tillman, Amy; Wittes, Janet; Pappas, Julie; Elci, Okan; Marshall, Kathleen A; McCague, Sarah; Reichert, Hannah; Davis, Maria; Simonelli, Francesca; Leroy, Bart P; Wright, J Fraser; High, Katherine A; Bennett, Jean.: Efficacy, Safety, and Durability of Voretigene Neparvovec-rzyl in RPE65 Mutation-Associated Inherited Retinal Dystrophy: Results of Phase 1 and 3 Trials. Ophthalmology 126 (9): 1273-1285,2019.
Aleman, Tomas S; Uyhazi, Katherine E; Serrano, Leona W; Vasireddy, Vidyullatha; Bowman, Scott J; Ammar, Michael J; Pearson, Denise J; Maguire, Albert M; Bennett, Jean.: RDH12 Mutations Cause a Severe Retinal Degeneration With Relatively Spared Rod Function. Investigative Ophthalmology & Visual Science 59 (12): 5225-5236,2018.
Silson, Edward H; Aleman, Tomas S; Willett, Aimee; Serrano, Leona W; Pearson, Denise J; Rauschecker, Andreas M; Maguire, Albert M; Baker, Chris I; Bennett, Jean; Ashtari, Manzar.: Comparing Clinical Perimetry and Population Receptive Field Measures in Patients with Choroideremia. Investigative Ophthalmology & Visual Science 59 (8): 3249-3258,2018.
Song, Ji Yun; Aravand, Puya; Nikonov, Sergei; Leo, Lanfranco; Lyubarsky, Arkady; Bennicelli, Jeannette L; Pan, Jieyan; Wei, Zhangyong; Shpylchak, Ivan; Herrera, Pamela; Bennett, Daniel J; Commins, Nicoletta; Maguire, Albert M; Pham, Jennifer; den Hollander, Anneke I; Cremers, Frans P M; Koenekoop, Robert K; Roepman, Ronald; Nishina, Patsy; Zhou, Shangzhen; Pan, Wei; Ying, Gui-Shuang; Aleman, Tomas S; de Melo, Jimmy; McNamara, Ilan; Sun, Junwei; Mills, Jason; Bennett, Jean.: Amelioration of Neurosensory Structure and Function in Animal and Cellular Models of a Congenital Blindness. Molecular Therapy 26 (6): 1581-1593,2018.
Russell, Stephen; Bennett, Jean; Wellman, Jennifer A; Chung, Daniel C; Yu, Zi-Fan; Tillman, Amy; Wittes, Janet; Pappas, Julie; Elci, Okan; McCague, Sarah; Cross, Dominique; Marshall, Kathleen A; Walshire, Jean; Kehoe, Taylor L; Reichert, Hannah; Davis, Maria; Raffini, Leslie; George, Lindsey A; Hudson, F Parker; Dingfield, Laura; Zhu, Xiaosong; Haller, Julia A; Sohn, Elliott H; Mahajan, Vinit B; Pfeifer, Wanda; Weckmann, Michelle; Johnson, Chris; Gewaily, Dina; Drack, Arlene; Stone, Edwin; Wachtel, Katie; Simonelli, Francesca; Leroy, Bart P; Wright, J Fraser; High, Katherine A; Maguire, Albert M.: Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial. Lancet 390 : 849-860,2017.
Ashtari, Manzar; Nikonova, Elena S; Marshall, Kathleen A; Young, Gloria J; Aravand, Puya; Pan, Wei; Ying, Gui-Shuang; Willett, Aimee E; Mahmoudian, Mani; Maguire, Albert M; Bennett, Jean.: The Role of the Human Visual Cortex in Assessment of the Long-Term Durability of Retinal Gene Therapy in Follow-on RPE65 Clinical Trial Patients. Ophthalmology 124 (6): 873-883,2017.
Parikh, Rupin N; Traband, Anastasia; Kolomeyer, Anton M; VanderBeek, Brian L; Kim, Benjamin J; Maguire, Albert M; Brucker, Alexander J.: Intravitreal Bevacizumab for the Treatment of Vitreous Hemorrhage Due to Proliferative Diabetic Retinopathy. American Journal of Ophthalmology 176 : 194-202,2017.
Aleman, Tomas S; Han, Grace; Serrano, Leona W; Fuerst, Nicole M; Charlson, Emily S; Pearson, Denise J; Chung, Daniel C; Traband, Anastasia; Pan, Wei; Ying, Gui-Shuang; Bennett, Jean; Maguire, Albert M; Morgan, Jessica I W.: Natural History of the Central Structural Abnormalities in Choroideremia: A Prospective Cross-Sectional Study. Ophthalmology 124 (3): 359-373,2017.
Ramachandran Pavitra, Lee Vivian, Wei Zhangyong, Song Ji Yun, Casal Giulia, Cronin Therese, Willett Keirnan, Huckfeldt Rachel, Morgan Jessica I W, Aleman Tomas S, Maguire Albert M, Bennett Jean: Evaluation of dose and safety of AAV7m8 and AAV8BP2 in the non-human primate retina. Human gene therapy : 2016.
Academic Contact Information
Scheie Eye Institute
Department of Ophthalmology
University of Pennsylvania
51 North 39th Street
Philadelphia,
PA
19104
Patient appointments: 800-789-7366